Search for Clinical Trial Results
Inclusion Body Myopathy 2 - 14 Studies Found
Status | Study |
Enrolling by invitation |
Study Name: Study to Evaluate the Safety and Efficacy of Ace-ER Tablets in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy Condition:
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Recruiting |
Study Name: A Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER) Tablets in GNE Myopathy (GNEM) (Also Known as Hereditary Inclusion Body Myopathy (HIBM)) Patients With Severe Ambulatory Impairment Condition:
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Completed |
Study Name: Natural History in CCFDN and IBM Syndromes Condition:
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Active, not recruiting |
Study Name: Clinical, Biological and NMR Outcome Measures Study for Hereditary Inclusion Body Myopathy Due to Mutation of UDP-N-acetylglucosamine 2-epimerase/N-acetylmannosamine Kinase Gene (GNE) Condition: HIBM Date: 2014-04-08 Interventions:
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